Addressing Challenges in Developing Treatments for Inherited Retinal Diseases: Recommendations From the Third Monaciano Symposium

on behalf of the Monaciano Consortium

doi:10.1167/tvst.14.8.37

Addressing Challenges in Developing Treatments for Inherited Retinal Diseases: Recommendations From the Third Monaciano Symposium

on behalf of the Monaciano Consortium

Jerry M. Wallace School of Osteopathic Medicine

University of Michigan Medical School
King’s College London
IRCCS Bambino Gesù Children’s Hospital
Duke University School of Medicine
Sorbonne Université
Centre Hospitalier National D’Ophtalmologie des Quinze Vingts
Telethon Institute of Genetics and Medicine
UCL Institute of Ophthalmology
Hadassah-Hebrew University Medical Center
Retina Foundation of the Southwest
University of Pennsylvania
University of Texas Health Science Center-Houston
University of California San Francisco
University of California-Berkeley
Israelitic Hospital
Hospital for Sick Children
Inc.
University of North Carolina School of Medicine
University of California-Irvine
Ghent University Hospital & Ghent University
Children’s Hospital of Philadelphia
University of Trieste
Moorfields Eye Hospital NHS Foundation Trust
Oregon Health Science Center
Michigan State University
Beth Israel Deaconess Medical Center and Harvard Medical School
Fondation Ophtalmologique
University of Pittsburgh School of Medicine
University of California-Davis School of Medicine
CNR Neuroscience Institute
University of Washington

Research output: Contribution to journal › Article › peer-review

Original language	English
Article number	37
Journal	Translational Vision Science and Technology
Volume	14
Issue number	8
DOIs	https://doi.org/10.1167/tvst.14.8.37
State	Published - Aug 2025

ASJC Scopus Subject Areas

Biomedical Engineering
Ophthalmology

Keywords

clinical trials
gene therapy
inherited blindness
outcome measures
patient support

Access to Document

10.1167/tvst.14.8.37

Cite this

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title = "Addressing Challenges in Developing Treatments for Inherited Retinal Diseases: Recommendations From the Third Monaciano Symposium",

keywords = "clinical trials, gene therapy, inherited blindness, outcome measures, patient support",

author = "\{on behalf of the Monaciano Consortium\} and Thompson, \{Debra A.\} and Jayasundera, \{K. Thiran\} and Oleg Alekseev and Ali, \{Robin R.\} and Alessia Amato and Arshavsky, \{Vadim Y.\} and Audo, \{Isabelle S.\} and Alberto Auricchio and Bainbridge, \{James W.B.\} and Eyal Banin and Besirli, \{Cagri G.\} and Birch, \{David G.\} and Branham, \{Kari E.\} and Cideciyan, \{Artur V.\} and Daiger, \{Stephen P.\} and Duncan, \{Jacque L.\} and Fahim, \{Abigail T.\} and Flannery, \{John G.\} and Roberto Gattegna and Heckenlively, \{John R.\} and Elise H{\'e}on and Alessandro Iannaccone and Khan, \{Naheed W.\} and Samer Khateb and Klassen, \{Henry J.\} and Leroy, \{Bart P.\} and Dario Marangoni and Michel Michaelides and Musch, \{David C.\} and Pennesi, \{Mark E.\} and Petersen-Jones, \{Simon M.\} and Pierce, \{Eric A.\} and Rao, \{Rajesh C.\} and Sahel, \{Jos{\'e} Alain\} and Sieving, \{Paul A.\} and Enrica Strettoi and Strong, \{Cameron R.\} and Wubben, \{Thomas J.\} and Paul Yang and Zacks, \{David N.\}",

note = "Publisher Copyright: {\textcopyright} 2025 The Authors.",

year = "2025",

month = aug,

doi = "10.1167/tvst.14.8.37",

language = "English",

volume = "14",

journal = "Translational Vision Science and Technology",

issn = "2164-2591",

number = "8",

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T1 - Addressing Challenges in Developing Treatments for Inherited Retinal Diseases

T2 - Recommendations From the Third Monaciano Symposium

AU - on behalf of the Monaciano Consortium

AU - Thompson, Debra A.

AU - Jayasundera, K. Thiran

AU - Alekseev, Oleg

AU - Ali, Robin R.

AU - Amato, Alessia

AU - Arshavsky, Vadim Y.

AU - Audo, Isabelle S.

AU - Auricchio, Alberto

AU - Bainbridge, James W.B.

AU - Banin, Eyal

AU - Besirli, Cagri G.

AU - Birch, David G.

AU - Branham, Kari E.

AU - Cideciyan, Artur V.

AU - Daiger, Stephen P.

AU - Duncan, Jacque L.

AU - Fahim, Abigail T.

AU - Flannery, John G.

AU - Gattegna, Roberto

AU - Heckenlively, John R.

AU - Héon, Elise

AU - Iannaccone, Alessandro

AU - Khan, Naheed W.

AU - Khateb, Samer

AU - Klassen, Henry J.

AU - Leroy, Bart P.

AU - Marangoni, Dario

AU - Michaelides, Michel

AU - Musch, David C.

AU - Pennesi, Mark E.

AU - Petersen-Jones, Simon M.

AU - Pierce, Eric A.

AU - Rao, Rajesh C.

AU - Sahel, José Alain

AU - Sieving, Paul A.

AU - Strettoi, Enrica

AU - Strong, Cameron R.

AU - Wubben, Thomas J.

AU - Yang, Paul

AU - Zacks, David N.

PY - 2025/8

Y1 - 2025/8

KW - clinical trials

KW - gene therapy

KW - inherited blindness

KW - outcome measures

KW - patient support

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UR - https://www.scopus.com/pages/publications/105015062492#tab=citedBy

U2 - 10.1167/tvst.14.8.37

DO - 10.1167/tvst.14.8.37

M3 - Article

C2 - 40862658

AN - SCOPUS:105015062492

SN - 2164-2591

VL - 14

JO - Translational Vision Science and Technology

JF - Translational Vision Science and Technology

IS - 8

M1 - 37

ER -

Addressing Challenges in Developing Treatments for Inherited Retinal Diseases: Recommendations From the Third Monaciano Symposium

ASJC Scopus Subject Areas

Keywords

Access to Document

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